Häufig gestellte Fragen

What is Etranacogene Dezaparvovec used for?

This gene therapy delivers a working copy of the factor IX gene into liver cells using a viral vector, enabling the body to produce its own clotting factor. It offers a potentially long-lasting treatment for hemophilia B.

How does Etranacogene Dezaparvovec work?

Delivers functional copies of a gene to target cells using a viral vector, restoring expression of the deficient protein and correcting the underlying genetic defect.

Is Etranacogene Dezaparvovec an approved drug?

Yes, Etranacogene Dezaparvovec is an approved drug. It has reached clinical phase 4. It is classified as a Gene.

{# References & Data Sources section for drug detail pages. Renders standard pharmacological database links plus the drug's data_sources field. #}

References & Data Sources

• ChEMBL — European Bioinformatics Institute (EBI). CHEMBL5095451. Open-access bioactivity database.

Data aggregated from publicly available pharmacological databases. Last updated 2026-02-27.