Miglustat
This oral medication reduces the production of certain fatty substances that accumulate harmfully in cells in people with specific inherited enzyme deficiency disorders. It is used to treat Gaucher disease and Niemann-Pick type C disease.
Peso molecular
219,2800 g/mol
LogP
-0,60
TPSA
84,20 Ų
Regla de cinco de Lipinski
Cumple
Pharmacokinetics (PK)
Pharmacodynamics (PD)
Estructura 2D
Cite this structure
Embed this structure
SMILES
CCCCN1C[C@H](O)[C@@H](O)[C@H](O)[C@H]1CO
InChI
InChI=1S/C10H21NO4/c1-2-3-4-11-5-8(13)10(15)9(14)7(11)6-12/h7-10,12-15H,2-6H2,1H3/t7-,8+,9-,10-/m1/s1
Molecular Formula
C10H21NO4
HBD / HBA
4 / 5
Enlaces Rotables
4
Átomos Pesados
15
No targets recorded
Target interaction data is not yet available for this drug.
No interactions recorded
Drug interaction data is not yet available for this compound.
No side effects recorded
Side effect data is not yet available for this drug.
Preguntas frecuentes
This oral medication reduces the production of certain fatty substances that accumulate harmfully in cells in people with specific inherited enzyme deficiency disorders. It is used to treat Gaucher disease and Niemann-Pick type C disease.
Yes, Miglustat is an approved drug. It has reached clinical phase 4. It is classified as a Small molecule.
References & Data Sources
- ChEMBL — European Bioinformatics Institute (EBI). CHEMBL1029. Open-access bioactivity database.
- PubChem — National Center for Biotechnology Information (NCBI). CID 51634. Chemical information database.
Data aggregated from publicly available pharmacological databases. Last updated 2026-03-28.
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