Часто задаваемые вопросы

What is Eplontersen Sodium used for?

This RNA-targeted therapy reduces the production of a harmful protein called transthyretin that builds up and damages the heart and nerves in people with a rare inherited condition. It is given as a subcutaneous injection.

How does Eplontersen Sodium work?

Stabilizes the transthyretin (TTR) protein tetramer, preventing its dissociation into monomers that misfold and aggregate into amyloid fibrils in cardiac tissue.

Is Eplontersen Sodium an approved drug?

Yes, Eplontersen Sodium is an approved drug. It has reached clinical phase 4. It is classified as a Oligonucleotide.

{# References & Data Sources section for drug detail pages. Renders standard pharmacological database links plus the drug's data_sources field. #}

References & Data Sources

• ChEMBL — European Bioinformatics Institute (EBI). CHEMBL4594335. Open-access bioactivity database.

Data aggregated from publicly available pharmacological databases. Last updated 2026-02-27.