Olipudase Alfa
An enzyme replacement therapy for a rare inherited disease called acid sphingomyelinase deficiency, in which harmful lipids accumulate in the liver, spleen, and lungs. Regular infusions help break down these accumulated substances and improve organ function.
Mechanism of Action
Provides exogenous replacement of the deficient or absent enzyme, enabling the metabolic processing of accumulated substrates and restoring normal metabolic function.
Pharmacokinetics (PK)
Pharmacodynamics (PD)
Provides exogenous replacement of the deficient or absent enzyme, enabling the metabolic processing of accumulated substrates and restoring normal metabolic function.
HBD / HBA
- / -
No targets recorded
Target interaction data is not yet available for this drug.
No interactions recorded
Drug interaction data is not yet available for this compound.
No side effects recorded
Side effect data is not yet available for this drug.
Frequently Asked Questions
An enzyme replacement therapy for a rare inherited disease called acid sphingomyelinase deficiency, in which harmful lipids accumulate in the liver, spleen, and lungs. Regular infusions help break down these accumulated substances and improve organ function.
Provides exogenous replacement of the deficient or absent enzyme, enabling the metabolic processing of accumulated substrates and restoring normal metabolic function.
Yes, Olipudase Alfa is an approved drug. It has reached clinical phase 4. It is classified as a Enzyme.
References & Data Sources
- ChEMBL — European Bioinformatics Institute (EBI). CHEMBL3707358. Open-access bioactivity database.
Data aggregated from publicly available pharmacological databases. Last updated 2026-02-27.
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