Fidanacogene Elaparvovec

CHEMBL3990034 Phase 4 Aprovado Gene
Half-Life
Bioavailability
Protein Binding
Molecular Weight
g/mol
LogP
Phase
4

A gene therapy used to treat adults with moderately severe to severe hemophilia B (a hereditary bleeding disorder). It works by delivering a functional copy of the gene needed to produce clotting factor IX, potentially providing long-term bleeding control after a single treatment.

Mecanismo de Ação

Delivers functional copies of a gene to target cells using a viral vector, restoring expression of the deficient protein and correcting the underlying genetic defect.

Pharmacokinetics (PK)

Pharmacodynamics (PD)

Mecanismo

Delivers functional copies of a gene to target cells using a viral vector, restoring expression of the deficient protein and correcting the underlying genetic defect.

HBD / HBA

- / -

No targets recorded

Target interaction data is not yet available for this drug.

No interactions recorded

Drug interaction data is not yet available for this compound.

No side effects recorded

Side effect data is not yet available for this drug.

Perguntas frequentes

A gene therapy used to treat adults with moderately severe to severe hemophilia B (a hereditary bleeding disorder). It works by delivering a functional copy of the gene needed to produce clotting factor IX, potentially providing long-term bleeding control after a single treatment.

Delivers functional copies of a gene to target cells using a viral vector, restoring expression of the deficient protein and correcting the underlying genetic defect.

Yes, Fidanacogene Elaparvovec is an approved drug. It has reached clinical phase 4. It is classified as a Gene.

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References & Data Sources

  • ChEMBL — European Bioinformatics Institute (EBI). CHEMBL3990034. Open-access bioactivity database.

Data aggregated from publicly available pharmacological databases. Last updated 2026-02-27.

Aviso Médico

This content is for educational and informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment. Always consult a qualified healthcare provider before making medication decisions.

Data sources: ChEMBL, PubChem, DailyMed.